Rare Diseases Symptoms Automatic Extraction
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A random Abstract
Our Project
Our Team
Recent trends of polymer mediated liposomal gene delivery system.
[x-linked adrenoleukodystrophy]
Advancement
in
the
gene
delivery
system
have
resulted
in
clinical
successes
in
gene
therapy
for
patients
with
several
genetic
diseases
,
such
as
immunodeficiency
diseases
,
X-
linked
adrenoleukodystrophy
(
X-
ALD
)
blindness
,
thalassemia
,
and
many
more
.
Among
various
delivery
systems
,
liposomal
mediated
gene
delivery
route
is
offering
great
promises
for
gene
therapy
.
This
review
is
an
attempt
to
depict
a
portrait
about
the
polymer
based
liposomal
gene
delivery
systems
and
their
future
applications
.
Herein
,
we
have
discussed
in
detail
the
characteristics
of
liposome
,
importance
of
polymer
for
liposome
formulation
,
gene
delivery
,
and
future
direction
of
liposome
based
gene
delivery
as
a
whole
.
Diseases
Validation
Diseases presenting
"blindness"
symptom
aniridia
canavan disease
coats disease
cohen syndrome
congenital toxoplasmosis
cystinuria
dracunculiasis
fabry disease
gm1 gangliosidosis
junctional epidermolysis bullosa
kallmann syndrome
lamellar ichthyosis
neonatal adrenoleukodystrophy
oculocutaneous albinism
x-linked adrenoleukodystrophy
This symptom has already been validated